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1:03
YouTube
Cystic Fibrosis Foundation
CF Foundation | Gene Transfer
This video animation shows how gene transfer -- a type of gene therapy -- might one day be used to cure cystic fibrosis. This process would involve introducing a healthy CFTR gene into a person with CF in order to produce functional CFTR protein. Cystic fibrosis is caused by mutations in the CFTR gene that result in the production of a ...
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